06. March 2027
11:30 - 13:30 o'clock
Room: still open
Session 16 - The changing panorama of treatment
Chairs:
P. Huppke, NN
Themen:
- RNA Editing
- Update MeCP2 reactivation
- Trofinetide – first approved medication to treat Rett syndrome (J. Neul)
- Update Gene Therapy and preliminary results (Taysha)
- Update Gene Therapy and preliminary results (Neurogene)